Limb Girdle Muscular Dystrophy Consortium Forms to Prepare for Clinical Trials

Big news for Limb Girdle Muscular Dystrophies (LGMDs)! The Muscular Dystrophy Association (MDA) recently awarded a clinical research network grant to Dr. Nicholas Johnson, vice chair of research and associate professor of neurology at Virginia Commonwealth University, to establish an LGMD Consortium comprised of seven clinical sites. The goal of the consortium is to prepare for future clinical trials by studying the natural history (disease course) of LGMDs and identifying outcome assessments that will be used in trials to determine if a drug or intervention is working. The investigators will initially focus on four subtypes of LGMD, including LGMD2A/calpainopathy.

Click here to read the full announcement from the MDA!