C3 Scientific Conference 2018

On September 12 – 13, 2018, Coalition to Cure Calpain 3 hosted the “C3 Scientific Conference” in Arlington, Virginia.

In attendance were prominent neuromuscular clinicians, world renowned research scientists from academia and industry, and  representatives from various funding agencies. This included C3’s Scientific Advisory Board and C3 grant recipients.

The goal of the conference was to gather key experts for scientific discussion focused around increasing our understanding of LGMD2A and preparing for future clinical trials in order to accelerate the development of a therapy for this disease. The topics of the sessions included:
• Pre-clinical models for LGMD2A
• Registries and genetic testing
• Outcomes Assessments and biomarkers
• Muscle building
• Gene therapy and gene editing