Coalition to Cure Calpain 3 (C3) attended the 23rd International Annual Congress of the World Muscle Society, October 2-6 2018 in Mendoza, Argentina. Dr. Jennifer Levy, C3 Scientific Director, represented C3 and presented a poster detailing our mission, registry, and research grants program. Attendees include neuromuscular clinicians, academics, research scientists, and industry leaders from around the world. The Congress covered a variety of topics related to advances across the neuromuscular field, including development of treatments of neuromuscular disorders. Among the highlights:

Dr. Jennifer Levy (right), C3 Scientific Director, and Heather Hilsden (left), Project Manager Jain Foundation Clinical Outcome Study at the World Muscle Society poster session
Dr. Jennifer Levy (right), C3 Scientific Director, and Heather Hilsden (left), Project Manager Jain Foundation Clinical Outcome Study at the World Muscle Society poster session
  • R. El-Khoury, American University of Beirut Medical Center, Lebanon, showed data on the different mitochondria deficiencies observed in muscle biopsy samples from LGMD2A patients
  • Conrad Weihl, Washington University St. Louis, USA, demonstrated progress towards identifying the symptoms that affect the health and daily function of individuals with LGMD using a qualitative, patient-directed approach
  • Jerry Mendell presented updated results from Sarepta Therapeutics gene therapy micro-dystrophin trial to treat patients with Duchenne Muscular Dystrophy. They have observed efficient gene transfer and a favorable safety profile. Early results suggest functional improvements for the patients, however, this is a small data set and results still need to be confirmed with a larger trial

 

The next World Muscle Society Congress will be held October 1-5, 2019 in Copenhagen, Denmark.

C3 Presents at World Muscle Society Congress