On this day, C3 would like to take the opportunity to discuss the DRUG DEVELOPMENT PROCESS for rare diseases such as LGMD2A/R1. DISCOVERY: Drug development usually begins in the laboratory, where researchers seek to gain new insights into a disease process. With a
New “Voice of the Patient” report highlights unmet medical needs of six subtypes of LGMD, including LGMD2A/R1
Today, Coalition to Cure Calpain 3 joins five other LGMD patient organizations (collectively referred to as The LGMD Coalition*) to release the ‘Voice of the Patient Report’ summarizing outcomes from the September 2022 Externally-Led Patient Focused Drug Development Meeting (EL-PFDD).