Rare Disease Day takes place on the last day of February every year, with the goal of raising awareness about rare diseases and their impact on patients’ lives. Over 300 million people are living with one or more of over
Sarepta Community Update on LGMD programs
Sarepta Therapeutics recently published a Community Letter to share updates on their limb-girdle muscular dystrophy gene therapy programs. Click here to access the letter on Sarepta’s website.
New research grant aims to improve genetic diagnoses in individuals with CAPN3 mutations
Coalition to Cure Calpain 3 (C3) is pleased to announce a research grant has been awarded to Dr. Svetlana Gorokhova, working together with Dr. Marc Bartoli in the Translational Neuromyology Team, Marseille Medical Genetics Institute at Aix Marseille University. The
English
አማርኛ
العربية
简体中文
繁體中文
Dansk
Nederlands
Français
Deutsch
עִבְרִית
हिन्दी
Italiano
日本語
ភាសាខ្មែរ
한국어
كوردی
मराठी
Norsk bokmål
Polski
Português
ਪੰਜਾਬੀ
Русский
Español
Svenska
தமிழ்
తెలుగు
Türkçe